complex ethics of genetic engineering, including safety, social justice, and regulation, to understand how this technology ...

Scientists have identified mutated immune cell clones that could point to improved treatment for refractory celiac disease.

Ask scientists what gene editing tool is most needed to advance gene therapy, and they'd probably describe a system that's now close to realization in the labs of Samuel Sternberg at Columbia ...

A new gene editor takes advantage of CRISPR-associated proteins to insert whole genes into the genome, scientists report.

A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.

A blood test revealed toxic levels of ammonia building up in KJ’s body, threatening to damage his brain — a sign of an ...

“For more than a century, orange coat color in cats has been recognized as an exception to the genetic rules that explain ...

The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific gene mutation, doctors say.

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as ...

The technique used on a 9½-month-old boy with a rare condition has the potential to help people with thousands of other ...

Researchers at Kyushu University in Japan have pinpointed the X-linked mutation behind orange fur in house cats.

The “meow-tation” that gives ginger cats their distinct fur has been discovered. A small deletion in a gene on the ...