A standoff over Elevidys could have major consequences for Duchenne patients, gene therapy companies and the perception of ...

The FDA has placed multiple investigational gene therapy clinical trials on hold, signaling broader platform concerns.

Reeling from the deaths of two patients who took Duchenne muscular dystrophy gene therapy Elevidys, Sarepta is launching a ...

Sarepta Therapeutics is laying off 500 staffers, or 36% of its workforce, as part of a strategic restructuring aiming to save $400 million annually. | Sarepta Therapeutics has laid off 500 staffers, ...