News

Child treated with gene editing therapy for the first time by a team of Philadelphia doctors
A team of doctors at the Children's Hospital of Philadelphia and Penn Medicine treated a baby with a gene editing technology ...
Doctors successfully treated a baby with the first ever personalized gene-editing therapy
A team of doctors and scientists have successfully treated a rare genetic condition with the first-ever personalized ...
First Alert 4 on MSN16d
New gene therapy considered cure for Sickle Cell Disease being administered at St. Louis Children’s Hospital
A gene therapy recently approved by the FDA to treat patients with Sickle Cell Anemia is now being administered in St. Louis.
St. Louis Post-Dispatch24d
In a first for St. Louis, patient completes new gene therapy to cure sickle cell disease
Martin, 20, was the first patient in St. Louis and among the first across the country to receive a new gene therapy for sickle ... and friends made — full of pictures, encouraging notes and ...
Ars Technica5d
From birth to gene-edited in 6 months: Custom therapy breaks speed limits
News broke yesterday that researchers in Philadelphia appear to have successfully treated a 6-month-old baby boy, called KJ, with a personalized CRISPR gene-editing therapy. The treatment corrects ...
Wall Street Journal6d
A Gene-Editing Breakthrough Saves Infant With Rare Disease
An infant in Philadelphia has been successfully treated with a customized Crispr gene-editing therapy for a rare and deadly disease, doctors reported Thursday—a breakthrough in the futuristic ...
KERA News9d
Rowlett girl could help pioneer therapy for rare genetic disorder
The 11-year-old will be the first to receive an experimental antisense oligonucleotide gene therapy to treat NARS1 symptoms. “With her being the first, she’s going pioneer the way for a lot of ...
CBS News23d
First patient to receive gene therapy treatment developed at Children's Hospital of Philadelphia living pain-free
A new gene therapy developed at the Children's Hospital of Philadelphia has been approved by the FDA and is being used to transform lives. The first patient to receive this gene therapy after it ...
Hosted on MSN22d
US FDA approves first cell-based gene therapy for rare genetic skin disorder
(Reuters) -The U.S. Food and Drug Administration approved Abeona Therapeutics' gene therapy for a rare skin disorder on Tuesday. Shares of the Cleveland-based drugmaker rose 13% in premarket trading.