The researchers described the unprecedented speed of the oversight steps as being "through alternative procedures." In month ...

The Crispr therapy was tailored to the baby’s specific condition and could provide a template for others.

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new study ...

Ventura is expected to be back in court Friday for additional cross-examination. Earlier Thursday, the judge told Combs' defense team that unless there was a compelling reason, cross-examination ...

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases. Doctors say they constructed a bespoke gene ...

You can reach Jason on Signal at JasonMast.05. NEW ORLEANS — The mood at the annual meeting of the American Society of Cell and Gene Therapy isn’t amazing. The biotech market has been bad for ...

You can reach Megan on Signal at mmolteni.13. Leading trade organizations representing the makers of cell and gene therapies are calling for a 10-year international moratorium on the use of CRISPR ...

A flexible, intrinsically disordered region (IDR) in the TAF2 protein directs its movement between gene promoters and nuclear speckles, linking transcription initiation and RNA processing.

Gene therapies, which can be extremely expensive to develop, generally target more common disorders in part for simple financial reasons: more patients mean potentially more sales, which can help ...

Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec. AAN Evidence in Focus articles highlight the strength of the current ...