Spinal muscular atrophy with respiratory distress (SMARD) is a rare genetic condition that typically affects infants and children. It causes muscle weakness and breathing problems. Spinal muscular ...

Duchenne muscular dystrophy (DMD) is a muscle degeneration disorder caused by mutations affecting the dystrophin gene. Researchers show how a dual CRISPR RNA method restored dystrophin protein ...

What happens here matters everywhere. by Charlotte Schubert on January 25, 2023 at 9:01 pm January 25, 2023 at 9:46 pm From left: Myosana CEO Matthew Lumley, with co-founders Stanley Froehner and Nick ...