Scientists at the McGovern Institute and the Broad Institute of MIT and Harvard have reengineered a compact RNA-guided enzyme ...

At a gene therapy conference, there was excitement about the first correction of a genetic misspelling, along with questions ...

In a world first, a child diagnosed with a rare metabolic disorder has been successfully treated with a customized CRISPR ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...

Current setbacks cannot prevent gene-editing companies from advancing closer to “one-and-done” cures and new products.

“It’s terrific work,” said Erik Sontheimer, a gene editing researcher at UMass Chan Medical School. “It truly brings CRISPR genome editing into the n-of-1 regime.” The results may offer ...

A team of doctors and scientists have successfully treated a rare genetic condition with the first-ever personalized ...

Fyodor Urnov and Alexis Komor will be speakers at GEN’s 2025 virtual event, The State of CRISPR and Genome Editing, streaming on June 11 th.

Recent biotechnological innovations like genome — editing in crop breeding are seen as major achievements to address the challenges of food security and also to reduce the burden of agriculture to ...

Potential best-in-class extrahepatic in vivo gene editing with all-in-one delivery to the central nervous system (CNS) is a ...