News

Doctors successfully treated a baby with the first ever personalized gene-editing therapy
A team of doctors and scientists have successfully treated a rare genetic condition with the first-ever personalized ...
Child treated with gene editing therapy for the first time by a team of Philadelphia doctors
A team of doctors at the Children's Hospital of Philadelphia and Penn Medicine treated a baby with a gene editing technology ...
STAT5d
At gene therapy meeting, no one wants to talk about the Vinay Prasad (not) in the room
05. NEW ORLEANS — Last year, hundreds of people poured in to hear Peter Marks, the Food and Drug Administration’s head of biologics, speak at the American Society of Gene and Cell Therapy ...
First Alert 4 on MSN15d
New gene therapy considered cure for Sickle Cell Disease being administered at St. Louis Children’s Hospital
A gene therapy recently approved by the FDA to treat patients with Sickle Cell Anemia is now being administered in St. Louis.
STAT5d
Day 3 at ASGCT: Vinay Prasad speculation, screening newborns, promising data
You can reach Jason on Signal at JasonMast.05. NEW ORLEANS — Greetings from the home stretch of American Society of Gene and Cell Therapy conference, where everyone is still talking about Baby ...
GEN - Genetic Engineering and Biotechnology News7d
Mass Photometry Speeds Up Gene Therapy Manufacturing—No Purification Needed
Mass photometry enables rapid, purification-free quantification of rAAV vectors, offering a faster solution for gene therapy ...
Wall Street Journal5d
A Gene-Editing Breakthrough Saves Infant With Rare Disease
An infant in Philadelphia has been successfully treated with a customized Crispr gene-editing therapy for a rare and deadly disease, doctors reported Thursday—a breakthrough in the futuristic ...
CBS News22d
First patient to receive gene therapy treatment developed at Children's Hospital of Philadelphia living pain-free
A new gene therapy developed at the Children's Hospital of Philadelphia has been approved by the FDA and is being used to transform lives. The first patient to receive this gene therapy after it ...
The New England Journal of Medicine21d
Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1
The β 2 common integrin subunit CD18 is essential for leukocyte–endothelial adhesion and extravasation to inflamed or infected tissue. Damaging variants in ITGB2, which encodes CD18, cause ...
MedPage Today22d
FDA OKs New Gene Therapy for Debilitating Skin Condition
The FDA approved prademagene zamikeracel (Zevaskyn) for treating adults and children with the blistering wounds caused by recessive dystrophic epidermolysis bullosa (RDEB), Abeona Therapeutics ...